The Rich Family
Six-year-old Lily Rich was diagnosed with Autism at 2 years and her parents were told there was no cure. However, while exhibiting the characteristics of autism, the cause was actually a rare gene mutation. Not willing to accept that no treatment was possible, they have partnered with an innovative gene therapy platform called Rarebase to find an FDA approved repurposed drug that might treat Lily’s rare gene mutation. Rarebase leverages biology and cutting-edge artificial intelligence technology to rapidly discover and develop treatments for millions of people worldwide living with a rare disease.